Leveraging Preclinical Data to Ensure Successful Delivery of an AAV-based Gene Therapy After Transition into the Clinic
Time: 3:30 pm
day: Conference Day 2
Details:
- Overcoming barriers to efficient intravitreal delivery of AAV-based gene therapy to the retina
- Employing directed evolution in nonhuman primates to discover novel retinotropic AAV vectors for clinical gene therapy
- Exploring key translational research considerations to facilitate clinical trial development